Effectiveness of PCSK9 Inhibitors in Familial Hypercholesterolemia: Feasibility Study

Effectiveness of PCSK9 Inhibitors in Familial Hypercholesterolemia: Feasibility Study

Effectiveness of PCSK9 Inhibitors in Familial Hypercholesterolemia: Feasibility Study

HC0094_OS0011

Overview

Background
  • Proprotein convertase subtilisin/kexin type 9 inhibitors (PCSK9i) are a relatively novel class of drugs used in the treatment of familial hypercholesterolemia (FH), a genetic disorder characterized by lifelong elevated low-density lipoprotein cholesterol (LDL-C) levels and increased risk of premature atherosclerotic cardiovascular disease (ASCVD) and death.
  • However, data are limited on the real-world use and effectiveness of PCSK9i for FH in Canada.
Objectives
  • Part 1 objective (using CIHI data): To describe the utilization of PCSK9i and characteristics of patients who are prescribed these drugs in Canada.
  • Part 2 objectives (using CNODES provincial data source):
    • To determine the percentage of patients with FH who are achieving the public drug plans’ recommended treatment goal of at least 40% reduction in LDL-C during treatment with PCSK9i.
    • To estimate the incidence of major adverse cardiovascular events among patients with FH who are prescribed PCSK9i.

Manuscripts

Presentations

Project Team

Project Co-Lead
Scott Klarenbach
Project Co-Lead
Michael Paterson MSc
Methods Lead
Robert W. Platt PhD
Content Expert
Darren Lau
Steering Committee Liaison
Michael Paterson MSc
Research Assistant
Jason Randall
Research Assistant
Audray St-Jean MSc
Site Investigator
Michael Paterson MSc
Ontario
Site Investigator
Greg Carney BSc, PhD
British Columbia
Site Investigator
Karen Martins
Alberta
Site Investigator
Scott Klarenbach
Alberta
Analyst
Tarita Miller BSc
British Columbia
Analyst
Mani Liu
Alberta
Analyst
Huong Luu
Alberta
Analyst
Khanh Vu
Alberta